Niemann–Pick type C disease: cellular pathology and pharmacotherapy - Wheeler - 2020 - Journal of Neurochemistry - Wiley Online Library
2-Hydroxypropyl-gamma-cyclodextrin overcomes NPC1 deficiency by enhancing lysosome-ER association and autophagy | Scientific Reports
Investigation of 2-Hydroxypropyl-β-Cyclodextrin Treatment in a Neuronal-Like Cell Model of Niemann–Pick Type C Using Quantitative Proteomics | Journal of the American Society for Mass Spectrometry
Walgreen's Support Allows Our Twins with Niemann Pick Type C To Receive Cyclodextrin Treatments At Home | The Addi and Cassi Fund - Niemann Pick Type C
Penn Vet | Research Laboratory
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PDF] Oxidative Stress: A Pathogenic Mechanism for Niemann-Pick Type C Disease | Semantic Scholar
β-Cyclodextrin-threaded Biocleavable Polyrotaxanes Ameliorate Impaired Autophagic Flux in Niemann-Pick Type C Disease* - Journal of Biological Chemistry
Niemann-Pick C disease and mobilization of lysosomal cholesterol by cyclodextrin - ScienceDirect
Pluronic based β-cyclodextrin polyrotaxanes for treatment of Niemann-Pick Type C disease | Scientific Reports
IJMS | Free Full-Text | Neurodegeneration in Niemann–Pick Type C Disease: An Updated Review on Pharmacological and Non-Pharmacological Approaches to Counteract Brain and Cognitive Impairment
IJMS | Free Full-Text | In Vitro and In Vivo Evaluation of 6-O-α-Maltosyl-β- Cyclodextrin as a Potential Therapeutic Agent Against Niemann-Pick Disease Type C
Oxidative Stress: A Pathogenic Mechanism for Niemann-Pick Type C Disease
Niemann–Pick type C disease: cellular pathology and pharmacotherapy - Wheeler - 2020 - Journal of Neurochemistry - Wiley Online Library
A human iPSC-derived inducible neuronal model of Niemann-Pick disease, type C1 | BMC Biology | Full Text
Niemann–Pick disease - Wikipedia
Characterization of hydroxypropyl-beta-cyclodextrins used in the treatment of Niemann-Pick Disease type C1 | PLOS ONE
Investigation of 2-Hydroxypropyl-β-Cyclodextrin Treatment in a Neuronal-Like Cell Model of Niemann–Pick Type C Using Quantitative Proteomics | Journal of the American Society for Mass Spectrometry
Investigating the Mechanism of Cyclodextrins in the Treatment of Niemann‐ Pick Disease Type C Using Crosslinked 2‐Hydroxypropyl‐β‐cyclodextrin,Small - X-MOL
Niemann–Pick Disease Type C
Linear Cyclodextrin Polymer Prodrugs as Novel Therapeutics for Niemann-Pick Type C1 Disorder | Scientific Reports
Cyclodextrin News
Lysosomal storage disorder therapeutics — David Thompson Group
Cyclodextrin Shows Promise in Niemann-Pick Type C Disease
Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1–2 trial - The Lancet
Elucidating the mechanism of cyclodextrins in the treatment of Niemann-Pick Disease Type C using crosslinked 2-hydroxypropyl-β-cyclodextrin | bioRxiv
